Constantiam Biosciences and Cincinnati Children’s Collaborate to Accelerate First-in-Class Neuronopathic Gaucher Disease Therapies
Summary
Constantiam Biosciences and Cincinnati Children’s formed a strategic collaboration to advance first-in-class therapies for neuronopathic Gaucher disease. The deal includes an exclusive option for future licensing rights tied to small-molecule treatments and combines Cincinnati Children’s translational research with Constantiam’s RareScan functional genomics platform. Constantiam is also raising a seed round to support IND-enabling work and first-in-human trials. The arrangement aims to match therapeutic candidates to patient genotypes and reduce risk in rare-disease drug development.
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